HERO update (1)

Promising early results from the HERO Trial for MDS

Earlier this year, Alvin Luk attended the CRISPR Medicine Conference in Copenhagen to provide an update on the HERO clinical trial for MECP2 Duplication Syndrome. Alvin’s presentation is available for the community to watch on YouTube.

In this video, you’ll learn about Huidagene’s experimental CRISPR-Cas13 therapy, HG204, and see the progress in the first treated child, three months after receiving the investigational drug. Skip to minute 26:00 for video footage of the patient.

These early results are very encouraging and further suggest that restoring MeCP2 protein levels could be a promising strategy to tackle MDS.

A second child has already been treated with HG204, and up to six patients are expected to be enrolled sequentially in this trial in China.

To the video

Τελευταία νέα

14. Ιούνιος 2025

Αποτελέσματα έρευνας: MECP2 μιλάει

Έρευνα
Διαβάστε
2. Ιούνιος 2025

A new step forward in the search for a cure: UMass Chan Licenses siRNA Technology  

Έρευνα SiRNA
Διαβάστε
12. Μάρτιος 2025

Έναρξη προσλήψεων για την κλινική δοκιμή ATTUNE

Έρευνα ASO
Διαβάστε