HERO update (1)

Promising early results from the HERO Trial for MDS

Earlier this year, Alvin Luk attended the CRISPR Medicine Conference in Copenhagen to provide an update on the HERO clinical trial for MECP2 Duplication Syndrome. Alvin’s presentation is available for the community to watch on YouTube.

In this video, you’ll learn about Huidagene’s experimental CRISPR-Cas13 therapy, HG204, and see the progress in the first treated child, three months after receiving the investigational drug. Skip to minute 26:00 for video footage of the patient.

These early results are very encouraging and further suggest that restoring MeCP2 protein levels could be a promising strategy to tackle MDS.

A second child has already been treated with HG204, and up to six patients are expected to be enrolled sequentially in this trial in China.

To the video

Neueste Nachrichten

14. Juni 2025

Umfrageergebnisse: Die globale MECP2-Duplikations-Community spricht

Umfrage
Weiterlesen
2. Juni 2025

A new step forward in the search for a cure: UMass Chan Licenses siRNA Technology  

Forschung SiRNA
Weiterlesen
12. März 2025

Beginn der Rekrutierung für die klinische ATTUNE-Studie

Forschung ASO
Weiterlesen