HERO update (1)

Promising early results from the HERO Trial for MDS

Earlier this year, Alvin Luk attended the CRISPR Medicine Conference in Copenhagen to provide an update on the HERO clinical trial for MECP2 Duplication Syndrome. Alvin’s presentation is available for the community to watch on YouTube.

In this video, you’ll learn about Huidagene’s experimental CRISPR-Cas13 therapy, HG204, and see the progress in the first treated child, three months after receiving the investigational drug. Skip to minute 26:00 for video footage of the patient.

These early results are very encouraging and further suggest that restoring MeCP2 protein levels could be a promising strategy to tackle MDS.

A second child has already been treated with HG204, and up to six patients are expected to be enrolled sequentially in this trial in China.

To the video

Son Haberler

14. Haziran 2025

Anket sonuçları: Küresel MECP2 Duplikasyon topluluğu konuşuyor

Anket
Okuyun
2. Haziran 2025

A new step forward in the search for a cure: UMass Chan Licenses siRNA Technology  

Araştırma SiRNA
Okuyun
12. Mart 2025

ATTUNE klinik çalışması için hasta alımı başladı

Araştırma ASO
Okuyun