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14. June 2025

Survey results: The global MECP2 Duplication community speaks

Survey
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2. June 2025

A new step forward in the search for a cure: UMass Chan Licenses siRNA Technology  

Research SiRNA
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20. May 2025

Promising early results from the HERO Trial for MDS

CRISPR Cure Research
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12. March 2025

Start of recruitment for the ATTUNE clinical trial

Research ASO
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12. March 2025

Recruitment starts for HERO: CRISPR cas13-clinical trial for MDS

Research CRISPR
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29. August 2024

ION440: IONIS brings MDS community to the next level

ASO Cure Research
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3. April 2024

HuidaGene: Moving towards clinical trials for MDS

Research CRISPR Cure
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16. December 2023

Huidagene: A promising CRISPR-CAS13 technology from Shanghai (China)

CRISPR Cure Research
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17. January 2023

Assessing the Burden on Caregivers of MECP2 Duplication Syndrome

Publication
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