カテゴリー: ASO

Start of recruitment for the ATTUNE clinical trial

The ATTUNE trial is a Phase 1/2 clinical study sponsored by Ionis. It aims to evaluate ION440, an investigational Antisense Oligonucleotide (ASO) therapy designed to address the root cause of MECP2 Duplication Syndrome (MDS).

ION440: IONIS brings MDS community to the next level

Written by David and verified by Ionis Following Ionis’ recent announcement about the upcoming clinical trial, we aim to provide a clearer understanding of this trial. It is especially important for families considering enrolling their child to know what a clinical trial is, particularly in the context of rare diseases like MECP2 Duplication Syndrome (MDS). A clinical trial is a research study that investigates new potential treatments, assessing their safety and effects on humans. Clinical trials are often conducted as part of a larger clinical development program. A clinical development program is a series of clinical trials conducted in progressive phases (i.e., Phase 1-3) designed to determine whether new potential […]