{"id":3562,"date":"2025-06-02T08:54:11","date_gmt":"2025-06-02T06:54:11","guid":{"rendered":"https:\/\/remeds.org\/?p=3562"},"modified":"2025-11-14T09:26:07","modified_gmt":"2025-11-14T08:26:07","slug":"umass-licenses-sirna-mecp2-duplication-syndrome","status":"publish","type":"post","link":"https:\/\/remeds.org\/tr\/2025\/06\/02\/umass-licenses-sirna-mecp2-duplication-syndrome\/","title":{"rendered":"Tedavi aray\u0131\u015f\u0131nda yeni bir ad\u0131m: UMass Chan siRNA Teknolojisini Lisanslad\u0131 \u00a0"},"content":{"rendered":"<p>UMass Chan T\u0131p Okulu, umut vaat eden bir siRNA tabanl\u0131 teknolojiyi, MECP2 Duplikasyon Sendromu tedavisi olarak teknolojiyi ilerletmeye adanm\u0131\u015f bir startup \u015firketi olan M2DS'ye lisanslad\u0131. Bu, en ileri ara\u015ft\u0131rmalar\u0131n klinik ger\u00e7e\u011fe d\u00f6n\u00fc\u015ft\u00fcr\u00fclmesinde b\u00fcy\u00fck bir ad\u0131m.\".<a href=\"https:\/\/dupmecp2.eu\/recruitement-hero\/\"><\/a><\/p>\n\n\n\n<p>Teknoloji, Dr. Khvorova'n\u0131n laboratuvar\u0131nda geli\u015ftirildi ve proje Vignesh Hariharan taraf\u0131ndan y\u00fcr\u00fct\u00fcld\u00fc. Erken ara\u015ft\u0131rmalar Cure MDS ve Rett Sendromu Ara\u015ft\u0131rma G\u00fcveni'nden al\u0131nan fonlar sayesinde yap\u0131ld\u0131. Bu siRNA, MeCP2 proteininin a\u015f\u0131r\u0131 \u00fcretilmesinden sorumlu haberci RNA'y\u0131 hedefleyip par\u00e7alayarak \u00e7al\u0131\u015f\u0131r. <\/p>\n\n\n\n<p>Fare \u00e7al\u0131\u015fmalar\u0131nda, bir dozun beyne ve omurili\u011fe etkili bir \u015fekilde ula\u015ft\u0131\u011f\u0131 ve yaln\u0131zca y\u0131lda bir veya iki kez uygulanmas\u0131 gerekebilece\u011fi belirtiliyor. Bu teknolojinin M2DS'ye lisanslanmas\u0131yla, tedavi art\u0131k insan denemelerine do\u011fru ilerlemek i\u00e7in gereken deste\u011fi alabilece\u011fi bir yola giriyor. <\/p>\n\n\n\n<p>Ionis ve HuidaGene'den devam eden klinik denemelere ek olarak, bu d\u00f6n\u00fcm noktas\u0131, bu nadir ve karma\u015f\u0131k bozukluk i\u00e7in potansiyel tedaviler hatt\u0131na umut verici bir ek olabilir.<\/p>\n\n\n\n<p><\/p>\n\n\n\n<p><a href=\"https:\/\/bridge.umassmed.edu\/s\/news\/news-article\/umass-chan-licenses-sirna-therapeutics-for-mecp2-duplication-syndrome-MCMWKNCJYQ25CQHF5YITTOM757HU\">Bas\u0131n b\u00fcltenini g\u00f6r<\/a><\/p>\n\n\n\n<p><\/p>","protected":false},"excerpt":{"rendered":"<p>UMass Chan Medical School has licensed a promising siRNA-based technology to M2DS, a startup company dedicated to advancing the technology as a treatment for MECP2 Duplication Syndrome. This marks a major step forward in translating cutting-edge research into clinical reality. The technology was developed in the lab of Dr. Khvorova, with the project led by [&hellip;]<\/p>\n","protected":false},"author":114,"featured_media":3563,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_jf_save_progress":"","footnotes":""},"categories":[9,24],"tags":[],"class_list":["post-3562","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-research","category-sirna"],"_links":{"self":[{"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/posts\/3562","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/users\/114"}],"replies":[{"embeddable":true,"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/comments?post=3562"}],"version-history":[{"count":3,"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/posts\/3562\/revisions"}],"predecessor-version":[{"id":3567,"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/posts\/3562\/revisions\/3567"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/media\/3563"}],"wp:attachment":[{"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/media?parent=3562"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/categories?post=3562"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/remeds.org\/tr\/wp-json\/wp\/v2\/tags?post=3562"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}