{"id":3538,"date":"2025-05-20T08:38:37","date_gmt":"2025-05-20T06:38:37","guid":{"rendered":"https:\/\/remeds.org\/?p=3538"},"modified":"2025-09-10T08:52:55","modified_gmt":"2025-09-10T06:52:55","slug":"early-results-hero-trial","status":"publish","type":"post","link":"https:\/\/remeds.org\/nl\/2025\/05\/20\/early-results-hero-trial\/","title":{"rendered":"Veelbelovende vroege resultaten van de HERO-studie voor MDS"},"content":{"rendered":"<p>Eerder dit jaar woonde Alvin Luk de CRISPR Medicine Conference in Kopenhagen bij om een update te geven over de HERO-klinische proef voor MECP2-duplicatiesyndroom. Alvin's presentatie is beschikbaar voor de gemeenschap om te bekijken op YouTube.<\/p>\n\n\n\n<p>In deze video leert u meer over Huidagene's experimentele CRISPR-Cas13 therapie, <strong>HG204<\/strong>, en zie de vooruitgang bij het eerste behandelde kind, drie maanden na ontvangst van het experimentele geneesmiddel. Ga naar <strong>minuut 26:00<\/strong> voor videobeelden van de pati\u00ebnt.<\/p>\n\n\n\n<p>Deze vroege resultaten zijn zeer bemoedigend en suggereren verder dat het herstellen van de niveaus van MeCP2-eiwit een veelbelovende strategie zou kunnen zijn om MDS aan te pakken.<\/p>\n\n\n\n<p>Een tweede kind is reeds behandeld met HG204, en er wordt verwacht dat er in China maximaal zes pati\u00ebnten sequentieel aan deze studie zullen deelnemen.<\/p>\n\n\n\n<p><a href=\"https:\/\/dupmecp2.eu\/recruitement-hero\/\"><\/a><\/p>\n\n\n\n<figure class=\"wp-block-image size-large\"><img fetchpriority=\"high\" decoding=\"async\" width=\"1024\" height=\"560\" src=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1024x560.png\" alt=\"\" class=\"wp-image-3539\" srcset=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1024x560.png 1024w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-300x164.png 300w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-768x420.png 768w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1536x841.png 1536w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-18x10.png 18w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025.png 1842w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-gallery has-nested-images columns-default is-cropped wp-block-gallery-1 is-layout-flex wp-block-gallery-is-layout-flex\">\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"1024\" height=\"575\" data-id=\"3542\" src=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-1024x575.png\" alt=\"\" class=\"wp-image-3542\" srcset=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-1024x575.png 1024w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-300x168.png 300w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-768x431.png 768w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-1536x862.png 1536w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-18x10.png 18w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1.png 2006w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"1024\" height=\"576\" data-id=\"3544\" src=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1024x576.png\" alt=\"\" class=\"wp-image-3544\" srcset=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1024x576.png 1024w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-300x169.png 300w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-768x432.png 768w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1536x864.png 1536w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-18x10.png 18w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4.png 2008w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"575\" data-id=\"3541\" src=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-1024x575.png\" alt=\"\" class=\"wp-image-3541\" srcset=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-1024x575.png 1024w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-300x169.png 300w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-768x431.png 768w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-1536x863.png 1536w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-18x10.png 18w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5.png 2006w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n<\/figure>\n\n\n\n<p><a href=\"https:\/\/www.youtube.com\/watch?v=uVFNm1UWQv8\" data-type=\"link\" data-id=\"https:\/\/www.youtube.com\/watch?v=uVFNm1UWQv8\">Naar de video<\/a><\/p>\n\n\n\n<p><\/p>","protected":false},"excerpt":{"rendered":"<p>Earlier this year, Alvin Luk attended the CRISPR Medicine Conference in Copenhagen to provide an update on the HERO clinical trial for MECP2 Duplication Syndrome. Alvin\u2019s presentation is available for the community to watch on YouTube. In this video, you\u2019ll learn about Huidagene\u2019s experimental CRISPR-Cas13 therapy, HG204, and see the progress in the first treated [&hellip;]<\/p>\n","protected":false},"author":114,"featured_media":3553,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_jf_save_progress":"","footnotes":""},"categories":[12,10,9],"tags":[],"class_list":["post-3538","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-crispr","category-cure","category-research"],"_links":{"self":[{"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/posts\/3538","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/users\/114"}],"replies":[{"embeddable":true,"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/comments?post=3538"}],"version-history":[{"count":10,"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/posts\/3538\/revisions"}],"predecessor-version":[{"id":3559,"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/posts\/3538\/revisions\/3559"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/media\/3553"}],"wp:attachment":[{"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/media?parent=3538"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/categories?post=3538"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/remeds.org\/nl\/wp-json\/wp\/v2\/tags?post=3538"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}