{"id":3562,"date":"2025-06-02T08:54:11","date_gmt":"2025-06-02T06:54:11","guid":{"rendered":"https:\/\/remeds.org\/?p=3562"},"modified":"2025-11-14T09:26:07","modified_gmt":"2025-11-14T08:26:07","slug":"umass-licenses-sirna-mecp2-duplication-syndrome","status":"publish","type":"post","link":"https:\/\/remeds.org\/hu\/2025\/06\/02\/umass-licenses-sirna-mecp2-duplication-syndrome\/","title":{"rendered":"\u00dajabb l\u00e9p\u00e9s a gy\u00f3gym\u00f3d keres\u00e9se fel\u00e9: UMass Chan licenceli az siRNA technol\u00f3gi\u00e1t \u00a0"},"content":{"rendered":"<p>Az UMass Chan Orvosi Iskola b\u00e9rbe adta egy \u00edg\u00e9retes, siRNA-alap\u00fa technol\u00f3gi\u00e1j\u00e1t az M2DS nev\u0171 startup c\u00e9gnek, amely elk\u00f6telezett amellett, hogy a technol\u00f3gi\u00e1t a MECP2 duplik\u00e1ci\u00f3s szindr\u00f3ma kezel\u00e9s\u00e9re fejlessze. Ez jelent\u0151s el\u0151rel\u00e9p\u00e9st jelent a cs\u00facstechnol\u00f3gi\u00e1s kutat\u00e1sok klinikai val\u00f3s\u00e1gg\u00e1 t\u00f6rt\u00e9n\u0151 \u00e1t\u00fcltet\u00e9s\u00e9ben.<a href=\"https:\/\/dupmecp2.eu\/recruitement-hero\/\"><\/a><\/p>\n\n\n\n<p>A technol\u00f3gi\u00e1t Dr. Khvorova laborat\u00f3rium\u00e1ban fejlesztett\u00e9k ki, a projektet pedig Vignesh Hariharan vezette. A korai kutat\u00e1sokat a Cure MDS \u00e9s a Rett Syndrome Research Trust t\u00e1mogat\u00e1s\u00e1nak k\u00f6sz\u00f6nhet\u0151en v\u00e9gezt\u00e9k. Ez az siRNA a MeCP2 feh\u00e9rje t\u00faltermel\u00e9s\u00e9\u00e9rt felel\u0151s messenger RNS c\u00e9lba v\u00e9tel\u00e9vel \u00e9s lebont\u00e1s\u00e1val m\u0171k\u00f6dik. <\/p>\n\n\n\n<p>Eg\u00e9rvizsg\u00e1latokban egy adag hat\u00e9konyan eljutott az agyba \u00e9s a gerincvel\u0151be, \u00e9s esetleg csak \u00e9vi egyszeri vagy k\u00e9tszeri adagol\u00e1st ig\u00e9nyel. A technol\u00f3gia M2DS-nek t\u00f6rt\u00e9n\u0151 licencel\u00e9se r\u00e9v\u00e9n a ter\u00e1pia most olyan \u00fatra l\u00e9pett, ahol megkaphatja a hum\u00e1n vizsg\u00e1latok fel\u00e9 t\u00f6rt\u00e9n\u0151 elmozdul\u00e1shoz sz\u00fcks\u00e9ges t\u00e1mogat\u00e1st. <\/p>\n\n\n\n<p>Az Ionis \u00e9s a HuidaGene folyamatban l\u00e9v\u0151 klinikai vizsg\u00e1latai mellett ez a m\u00e9rf\u00f6ldk\u0151 \u00edg\u00e9retes kieg\u00e9sz\u00edt\u00e9st jelenthet a ritka \u00e9s \u00f6sszetett rendelleness\u00e9g potenci\u00e1lis kezel\u00e9seinek k\u00edn\u00e1lat\u00e1ban.<\/p>\n\n\n\n<p><\/p>\n\n\n\n<p><a href=\"https:\/\/bridge.umassmed.edu\/s\/news\/news-article\/umass-chan-licenses-sirna-therapeutics-for-mecp2-duplication-syndrome-MCMWKNCJYQ25CQHF5YITTOM757HU\">L\u00e1sd sajt\u00f3k\u00f6zlem\u00e9ny<\/a><\/p>\n\n\n\n<p><\/p>","protected":false},"excerpt":{"rendered":"<p>UMass Chan Medical School has licensed a promising siRNA-based technology to M2DS, a startup company dedicated to advancing the technology as a treatment for MECP2 Duplication Syndrome. This marks a major step forward in translating cutting-edge research into clinical reality. The technology was developed in the lab of Dr. Khvorova, with the project led by [&hellip;]<\/p>\n","protected":false},"author":114,"featured_media":3563,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_jf_save_progress":"","footnotes":""},"categories":[9,24],"tags":[],"class_list":["post-3562","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-research","category-sirna"],"_links":{"self":[{"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/posts\/3562","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/users\/114"}],"replies":[{"embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/comments?post=3562"}],"version-history":[{"count":3,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/posts\/3562\/revisions"}],"predecessor-version":[{"id":3567,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/posts\/3562\/revisions\/3567"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/media\/3563"}],"wp:attachment":[{"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/media?parent=3562"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/categories?post=3562"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/tags?post=3562"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}