{"id":3538,"date":"2025-05-20T08:38:37","date_gmt":"2025-05-20T06:38:37","guid":{"rendered":"https:\/\/remeds.org\/?p=3538"},"modified":"2025-09-10T08:52:55","modified_gmt":"2025-09-10T06:52:55","slug":"early-results-hero-trial","status":"publish","type":"post","link":"https:\/\/remeds.org\/hu\/2025\/05\/20\/early-results-hero-trial\/","title":{"rendered":"A HERO-pr\u00f3ba biztat\u00f3 korai eredm\u00e9nyei mielodiszpl\u00e1zi\u00e1s szindr\u00f3m\u00e1ban"},"content":{"rendered":"

Id\u00e9n \u00e9v elej\u00e9n Alvin Luk r\u00e9szt vett a CRISPR Medicine Conference konferenci\u00e1n Koppenh\u00e1g\u00e1ban, hogy besz\u00e1moljon a HERO klinikai vizsg\u00e1lat \u00e1ll\u00e1s\u00e1r\u00f3l a MECP2-duplik\u00e1ci\u00f3s szindr\u00f3ma eset\u00e9ben. Alvin el\u0151ad\u00e1sa el\u00e9rhet\u0151 a YouTube-on a k\u00f6z\u00f6ss\u00e9g sz\u00e1m\u00e1ra.<\/p>\n\n\n\n

Ebben a vide\u00f3ban megismerheti a Huidagene k\u00eds\u00e9rleti CRISPR-Cas13 ter\u00e1pi\u00e1j\u00e1t, HG204<\/strong>, \u00e9s n\u00e9zz\u00e9k meg az els\u0151 kezelt gyermek fejl\u0151d\u00e9s\u00e9t, h\u00e1rom h\u00f3nappal a k\u00eds\u00e9rleti gy\u00f3gyszer bev\u00e9tele ut\u00e1n. Ugr\u00e1s a 26:00 perc<\/strong> videofelv\u00e9telekhez a p\u00e1ciensr\u0151l.<\/p>\n\n\n\n

Ezek a korai eredm\u00e9nyek nagyon biztat\u00f3ak, \u00e9s tov\u00e1bb er\u0151s\u00edtik azt a felt\u00e9telez\u00e9st, hogy a MeCP2 feh\u00e9rjeszint helyre\u00e1ll\u00edt\u00e1sa \u00edg\u00e9retes strat\u00e9gia lehet az MDS lek\u00fczd\u00e9s\u00e9re.<\/p>\n\n\n\n

Egy m\u00e1sodik gyermeket m\u00e1r kezeltek HG204-gyel, \u00e9s v\u00e1rhat\u00f3an legfeljebb hat beteget vesznek fel egym\u00e1s ut\u00e1n ebben a k\u00ednai vizsg\u00e1latban.<\/p>\n\n\n\n

<\/a><\/p>\n\n\n\n

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A vide\u00f3hoz<\/a><\/p>\n\n\n\n

<\/p>","protected":false},"excerpt":{"rendered":"

Earlier this year, Alvin Luk attended the CRISPR Medicine Conference in Copenhagen to provide an update on the HERO clinical trial for MECP2 Duplication Syndrome. Alvin\u2019s presentation is available for the community to watch on YouTube. In this video, you\u2019ll learn about Huidagene\u2019s experimental CRISPR-Cas13 therapy, HG204, and see the progress in the first treated […]<\/p>\n","protected":false},"author":114,"featured_media":3553,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_jf_save_progress":"","footnotes":""},"categories":[12,10,9],"tags":[],"class_list":["post-3538","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-crispr","category-cure","category-research"],"_links":{"self":[{"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/posts\/3538","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/users\/114"}],"replies":[{"embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/comments?post=3538"}],"version-history":[{"count":10,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/posts\/3538\/revisions"}],"predecessor-version":[{"id":3559,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/posts\/3538\/revisions\/3559"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/media\/3553"}],"wp:attachment":[{"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/media?parent=3538"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/categories?post=3538"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/remeds.org\/hu\/wp-json\/wp\/v2\/tags?post=3538"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}