{"id":3538,"date":"2025-05-20T08:38:37","date_gmt":"2025-05-20T06:38:37","guid":{"rendered":"https:\/\/remeds.org\/?p=3538"},"modified":"2025-09-10T08:52:55","modified_gmt":"2025-09-10T06:52:55","slug":"early-results-hero-trial","status":"publish","type":"post","link":"https:\/\/remeds.org\/es\/2025\/05\/20\/early-results-hero-trial\/","title":{"rendered":"Resultados preliminares prometedores del ensayo HERO para SMD"},"content":{"rendered":"

A principios de este a\u00f1o, Alvin Luk asisti\u00f3 a la Conferencia de Medicina CRISPR en Copenhague para ofrecer una actualizaci\u00f3n sobre el ensayo cl\u00ednico HERO para el S\u00edndrome de Duplicaci\u00f3n MECP2. La presentaci\u00f3n de Alvin est\u00e1 disponible para que la comunidad la vea en YouTube.<\/p>\n\n\n\n

En este video, aprender\u00e1s sobre la terapia experimental CRISPR-Cas13 de Huidagene, HG204<\/strong>, y ver el progreso en el primer ni\u00f1o tratado, tres meses despu\u00e9s de recibir el f\u00e1rmaco experimental. Saltar a minuto 26:00<\/strong> para metraje de video del paciente.<\/p>\n\n\n\n

Estos resultados iniciales son muy alentadores y sugieren adem\u00e1s que restaurar los niveles de prote\u00edna MeCP2 podr\u00eda ser una estrategia prometedora para abordar el s\u00edndrome de Rett.<\/p>\n\n\n\n

Un segundo ni\u00f1o ya ha sido tratado con HG204, y se espera que hasta seis pacientes se inscriban secuencialmente en este ensayo en China.<\/p>\n\n\n\n

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Al video<\/a><\/p>\n\n\n\n

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Earlier this year, Alvin Luk attended the CRISPR Medicine Conference in Copenhagen to provide an update on the HERO clinical trial for MECP2 Duplication Syndrome. Alvin\u2019s presentation is available for the community to watch on YouTube. In this video, you\u2019ll learn about Huidagene\u2019s experimental CRISPR-Cas13 therapy, HG204, and see the progress in the first treated […]<\/p>\n","protected":false},"author":114,"featured_media":3553,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_jf_save_progress":"","footnotes":""},"categories":[12,10,9],"tags":[],"class_list":["post-3538","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-crispr","category-cure","category-research"],"_links":{"self":[{"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/posts\/3538","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/users\/114"}],"replies":[{"embeddable":true,"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/comments?post=3538"}],"version-history":[{"count":10,"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/posts\/3538\/revisions"}],"predecessor-version":[{"id":3559,"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/posts\/3538\/revisions\/3559"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/media\/3553"}],"wp:attachment":[{"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/media?parent=3538"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/categories?post=3538"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/remeds.org\/es\/wp-json\/wp\/v2\/tags?post=3538"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}