{"id":3538,"date":"2025-05-20T08:38:37","date_gmt":"2025-05-20T06:38:37","guid":{"rendered":"https:\/\/remeds.org\/?p=3538"},"modified":"2025-09-10T08:52:55","modified_gmt":"2025-09-10T06:52:55","slug":"early-results-hero-trial","status":"publish","type":"post","link":"https:\/\/remeds.org\/el\/2025\/05\/20\/early-results-hero-trial\/","title":{"rendered":"\u0395\u03bb\u03c0\u03b9\u03b4\u03bf\u03c6\u03cc\u03c1\u03b1 \u03c0\u03c1\u03ce\u03c4\u03b1 \u03b1\u03c0\u03bf\u03c4\u03b5\u03bb\u03ad\u03c3\u03bc\u03b1\u03c4\u03b1 \u03b1\u03c0\u03cc \u03c4\u03b7 \u0394\u03bf\u03ba\u03b9\u03bc\u03ae HERO \u03b3\u03b9\u03b1 \u03c4\u03bf MDS"},"content":{"rendered":"<p>\u039d\u03c9\u03c1\u03af\u03c4\u03b5\u03c1\u03b1 \u03c6\u03ad\u03c4\u03bf\u03c2, \u03bf Alvin Luk \u03c0\u03b1\u03c1\u03b1\u03ba\u03bf\u03bb\u03bf\u03cd\u03b8\u03b7\u03c3\u03b5 \u03c4\u03bf \u03a3\u03c5\u03bd\u03ad\u03b4\u03c1\u03b9\u03bf \u0399\u03b1\u03c4\u03c1\u03b9\u03ba\u03ae\u03c2 CRISPR \u03c3\u03c4\u03b7\u03bd \u039a\u03bf\u03c0\u03b5\u03b3\u03c7\u03ac\u03b3\u03b7 \u03b3\u03b9\u03b1 \u03bd\u03b1 \u03b4\u03ce\u03c3\u03b5\u03b9 \u03bc\u03b9\u03b1 \u03b5\u03bd\u03b7\u03bc\u03ad\u03c1\u03c9\u03c3\u03b7 \u03c3\u03c7\u03b5\u03c4\u03b9\u03ba\u03ac \u03bc\u03b5 \u03c4\u03b7\u03bd \u03ba\u03bb\u03b9\u03bd\u03b9\u03ba\u03ae \u03b4\u03bf\u03ba\u03b9\u03bc\u03ae HERO \u03b3\u03b9\u03b1 \u03c4\u03bf \u03a3\u03cd\u03bd\u03b4\u03c1\u03bf\u03bc\u03bf \u0394\u03b9\u03c0\u03bb\u03b1\u03c3\u03b9\u03b1\u03c3\u03bc\u03bf\u03cd MECP2. \u0397 \u03c0\u03b1\u03c1\u03bf\u03c5\u03c3\u03af\u03b1\u03c3\u03b7 \u03c4\u03bf\u03c5 Alvin \u03b5\u03af\u03bd\u03b1\u03b9 \u03b4\u03b9\u03b1\u03b8\u03ad\u03c3\u03b9\u03bc\u03b7 \u03c3\u03c4\u03b7\u03bd \u03ba\u03bf\u03b9\u03bd\u03cc\u03c4\u03b7\u03c4\u03b1 \u03b3\u03b9\u03b1 \u03c0\u03b1\u03c1\u03b1\u03ba\u03bf\u03bb\u03bf\u03cd\u03b8\u03b7\u03c3\u03b7 \u03c3\u03c4\u03bf YouTube.<\/p>\n\n\n\n<p>\u03a3\u03b5 \u03b1\u03c5\u03c4\u03cc \u03c4\u03bf \u03b2\u03af\u03bd\u03c4\u03b5\u03bf, \u03b8\u03b1 \u03bc\u03ac\u03b8\u03b5\u03c4\u03b5 \u03b3\u03b9\u03b1 \u03c4\u03b7\u03bd \u03c0\u03b5\u03b9\u03c1\u03b1\u03bc\u03b1\u03c4\u03b9\u03ba\u03ae \u03b8\u03b5\u03c1\u03b1\u03c0\u03b5\u03af\u03b1 CRISPR-Cas13 \u03c4\u03b7\u03c2 Huidagene, <strong>HG204<\/strong>, \u03ba\u03b1\u03b9 \u03b4\u03b5\u03af\u03c4\u03b5 \u03c4\u03b7\u03bd \u03c0\u03c1\u03cc\u03bf\u03b4\u03bf \u03c3\u03c4\u03bf \u03c0\u03c1\u03ce\u03c4\u03bf \u03c0\u03b1\u03b9\u03b4\u03af \u03c0\u03bf\u03c5 \u03c5\u03c0\u03bf\u03b2\u03bb\u03ae\u03b8\u03b7\u03ba\u03b5 \u03c3\u03b5 \u03b8\u03b5\u03c1\u03b1\u03c0\u03b5\u03af\u03b1, \u03c4\u03c1\u03b5\u03b9\u03c2 \u03bc\u03ae\u03bd\u03b5\u03c2 \u03bc\u03b5\u03c4\u03ac \u03c4\u03b7 \u03c7\u03bf\u03c1\u03ae\u03b3\u03b7\u03c3\u03b7 \u03c4\u03bf\u03c5 \u03c0\u03b5\u03b9\u03c1\u03b1\u03bc\u03b1\u03c4\u03b9\u03ba\u03bf\u03cd \u03c6\u03b1\u03c1\u03bc\u03ac\u03ba\u03bf\u03c5. \u03a0\u03b1\u03c1\u03ac\u03bb\u03b5\u03b9\u03c8\u03b7 \u03c3\u03b5 <strong>26:00<\/strong> \u03b3\u03b9\u03b1 \u03b2.<\/p>\n\n\n\n<p>\u0391\u03c5\u03c4\u03ac \u03c4\u03b1 \u03c0\u03c1\u03ce\u03b9\u03bc\u03b1 \u03b1\u03c0\u03bf\u03c4\u03b5\u03bb\u03ad\u03c3\u03bc\u03b1\u03c4\u03b1 \u03b5\u03af\u03bd\u03b1\u03b9 \u03c0\u03bf\u03bb\u03cd \u03b5\u03bd\u03b8\u03b1\u03c1\u03c1\u03c5\u03bd\u03c4\u03b9\u03ba\u03ac \u03ba\u03b1\u03b9 \u03c5\u03c0\u03bf\u03b4\u03b7\u03bb\u03ce\u03bd\u03bf\u03c5\u03bd \u03c0\u03b5\u03c1\u03b1\u03b9\u03c4\u03ad\u03c1\u03c9 \u03cc\u03c4\u03b9 \u03b7 \u03b1\u03c0\u03bf\u03ba\u03b1\u03c4\u03ac\u03c3\u03c4\u03b1\u03c3\u03b7 \u03c4\u03c9\u03bd \u03b5\u03c0\u03b9\u03c0\u03ad\u03b4\u03c9\u03bd \u03c4\u03b7\u03c2 \u03c0\u03c1\u03c9\u03c4\u03b5\u0390\u03bd\u03b7\u03c2 MeCP2 \u03b8\u03b1 \u03bc\u03c0\u03bf\u03c1\u03bf\u03cd\u03c3\u03b5 \u03bd\u03b1 \u03b5\u03af\u03bd\u03b1\u03b9 \u03bc\u03b9\u03b1 \u03c0\u03bf\u03bb\u03bb\u03ac \u03c5\u03c0\u03bf\u03c3\u03c7\u03cc\u03bc\u03b5\u03bd\u03b7 \u03c3\u03c4\u03c1\u03b1\u03c4\u03b7\u03b3\u03b9\u03ba\u03ae \u03b3\u03b9\u03b1 \u03c4\u03b7\u03bd \u03b1\u03bd\u03c4\u03b9\u03bc\u03b5\u03c4\u03ce\u03c0\u03b9\u03c3\u03b7 \u03c4\u03bf\u03c5 MDS.<\/p>\n\n\n\n<p>\u0388\u03bd\u03b1 \u03b4\u03b5\u03cd\u03c4\u03b5\u03c1\u03bf \u03c0\u03b1\u03b9\u03b4\u03af \u03ad\u03c7\u03b5\u03b9 \u03ae\u03b4\u03b7 \u03b1\u03bd\u03c4\u03b9\u03bc\u03b5\u03c4\u03c9\u03c0\u03b9\u03c3\u03c4\u03b5\u03af \u03bc\u03b5 \u03c4\u03bf HG204, \u03ba\u03b1\u03b9 \u03b1\u03bd\u03b1\u03bc\u03ad\u03bd\u03b5\u03c4\u03b1\u03b9 \u03bd\u03b1 \u03b5\u03bd\u03c4\u03b1\u03c7\u03b8\u03bf\u03cd\u03bd \u03b4\u03b9\u03b1\u03b4\u03bf\u03c7\u03b9\u03ba\u03ac \u03ad\u03c9\u03c2 \u03ba\u03b1\u03b9 \u03ad\u03be\u03b9 \u03b1\u03c3\u03b8\u03b5\u03bd\u03b5\u03af\u03c2 \u03c3\u03b5 \u03b1\u03c5\u03c4\u03ae \u03c4\u03b7 \u03b4\u03bf\u03ba\u03b9\u03bc\u03ae \u03c3\u03c4\u03b7\u03bd \u039a\u03af\u03bd\u03b1.<\/p>\n\n\n\n<p><a href=\"https:\/\/dupmecp2.eu\/recruitement-hero\/\"><\/a><\/p>\n\n\n\n<figure class=\"wp-block-image size-large\"><img fetchpriority=\"high\" decoding=\"async\" width=\"1024\" height=\"560\" src=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1024x560.png\" alt=\"\" class=\"wp-image-3539\" srcset=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1024x560.png 1024w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-300x164.png 300w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-768x420.png 768w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1536x841.png 1536w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-18x10.png 18w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025.png 1842w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-gallery has-nested-images columns-default is-cropped wp-block-gallery-1 is-layout-flex wp-block-gallery-is-layout-flex\">\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"1024\" height=\"575\" data-id=\"3542\" src=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-1024x575.png\" alt=\"\" class=\"wp-image-3542\" srcset=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-1024x575.png 1024w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-300x168.png 300w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-768x431.png 768w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-1536x862.png 1536w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1-18x10.png 18w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-1.png 2006w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"1024\" height=\"576\" data-id=\"3544\" src=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1024x576.png\" alt=\"\" class=\"wp-image-3544\" srcset=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1024x576.png 1024w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-300x169.png 300w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-768x432.png 768w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-1536x864.png 1536w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4-18x10.png 18w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-4.png 2008w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"575\" data-id=\"3541\" src=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-1024x575.png\" alt=\"\" class=\"wp-image-3541\" srcset=\"https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-1024x575.png 1024w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-300x169.png 300w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-768x431.png 768w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-1536x863.png 1536w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5-18x10.png 18w, https:\/\/remeds.org\/wp-content\/uploads\/2025\/09\/HERO-CRISPR-conference-2025-5.png 2006w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n<\/figure>\n\n\n\n<p><a href=\"https:\/\/www.youtube.com\/watch?v=uVFNm1UWQv8\" data-type=\"link\" data-id=\"https:\/\/www.youtube.com\/watch?v=uVFNm1UWQv8\">\u03a3\u03c4\u03bf \u03b2\u03af\u03bd\u03c4\u03b5\u03bf<\/a><\/p>\n\n\n\n<p><\/p>","protected":false},"excerpt":{"rendered":"<p>Earlier this year, Alvin Luk attended the CRISPR Medicine Conference in Copenhagen to provide an update on the HERO clinical trial for MECP2 Duplication Syndrome. Alvin\u2019s presentation is available for the community to watch on YouTube. In this video, you\u2019ll learn about Huidagene\u2019s experimental CRISPR-Cas13 therapy, HG204, and see the progress in the first treated [&hellip;]<\/p>\n","protected":false},"author":114,"featured_media":3553,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_jf_save_progress":"","footnotes":""},"categories":[12,10,9],"tags":[],"class_list":["post-3538","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-crispr","category-cure","category-research"],"_links":{"self":[{"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/posts\/3538","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/users\/114"}],"replies":[{"embeddable":true,"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/comments?post=3538"}],"version-history":[{"count":10,"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/posts\/3538\/revisions"}],"predecessor-version":[{"id":3559,"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/posts\/3538\/revisions\/3559"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/media\/3553"}],"wp:attachment":[{"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/media?parent=3538"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/categories?post=3538"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/remeds.org\/el\/wp-json\/wp\/v2\/tags?post=3538"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}