{"id":3562,"date":"2025-06-02T08:54:11","date_gmt":"2025-06-02T06:54:11","guid":{"rendered":"https:\/\/remeds.org\/?p=3562"},"modified":"2025-11-14T09:26:07","modified_gmt":"2025-11-14T08:26:07","slug":"umass-licenses-sirna-mecp2-duplication-syndrome","status":"publish","type":"post","link":"https:\/\/remeds.org\/da\/2025\/06\/02\/umass-licenses-sirna-mecp2-duplication-syndrome\/","title":{"rendered":"Et nyt skridt fremad i jagten p\u00e5 en kur: UMass Chan licenserer siRNA-teknologi \u00a0"},"content":{"rendered":"<p class=\"wp-block-paragraph\">UMass Chan Medical School har licenseret en lovende siRNA-baseret teknologi til M2DS, en startup-virksomhed dedikeret til at videreudvikle teknologien som en behandling for MECP2 Duplikationssyndrom. Dette markerer et stort skridt fremad i at oms\u00e6tte banebrydende forskning til klinisk virkelighed.<a href=\"https:\/\/dupmecp2.eu\/recruitement-hero\/\"><\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Teknologien blev udviklet i Dr. Khvorovas laboratorium, med Vignesh Hariharan som projektleder. Tidlig forskning blev muliggjort takket v\u00e6re finansiering fra Cure MDS og Rett Syndrome Research Trust. Denne siRNA virker ved at m\u00e5lrette og nedbryde det messenger-RNA, der er ansvarligt for overproduktionen af MeCP2-proteinet. <\/p>\n\n\n\n<p class=\"wp-block-paragraph\">I museunders\u00f8gelser n\u00e5ede en dosis effektivt hjernen og rygmarven og kr\u00e6vede muligvis kun \u00e9n- eller to gange \u00e5rlig administration. Ved at licensere denne teknologi til M2DS, tr\u00e6der terapien nu ind p\u00e5 en vej, hvor den kan modtage den n\u00f8dvendige st\u00f8tte til at avancere mod humane fors\u00f8g. <\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Ud over de igangv\u00e6rende kliniske fors\u00f8g fra Ionis og HuidaGene kan denne milep\u00e6l tilf\u00f8je en lovende tilf\u00f8jelse til r\u00e6kken af potentielle behandlinger for denne sj\u00e6ldne og komplekse lidelse.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/bridge.umassmed.edu\/s\/news\/news-article\/umass-chan-licenses-sirna-therapeutics-for-mecp2-duplication-syndrome-MCMWKNCJYQ25CQHF5YITTOM757HU\">Se pressemeddelelse<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>UMass Chan Medical School has licensed a promising siRNA-based technology to M2DS, a startup company dedicated to advancing the technology as a treatment for MECP2 Duplication Syndrome. This marks a major step forward in translating cutting-edge research into clinical reality. The technology was developed in the lab of Dr. Khvorova, with the project led by [&hellip;]<\/p>\n","protected":false},"author":114,"featured_media":3563,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_jf_save_progress":"","footnotes":""},"categories":[9,24],"tags":[],"class_list":["post-3562","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-research","category-sirna"],"_links":{"self":[{"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/posts\/3562","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/users\/114"}],"replies":[{"embeddable":true,"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/comments?post=3562"}],"version-history":[{"count":3,"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/posts\/3562\/revisions"}],"predecessor-version":[{"id":3567,"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/posts\/3562\/revisions\/3567"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/media\/3563"}],"wp:attachment":[{"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/media?parent=3562"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/categories?post=3562"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/remeds.org\/da\/wp-json\/wp\/v2\/tags?post=3562"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}